

HY-177360 · 1 mg
MedChemExpress · Cat: HY-177360
Reach 3+ verified distributors
Manufacturer product page
medchemexpress.com/rna-splicing-modulator-4.html
Description
RNA splicing modulator-4 Compound A is an orally active, brain-penetrant and selective RNA splicing modulator. RNA splicing modulator-4 regulates the inclusion or exclusion of specific exons in precursor mRNA pre-mRNA by modulating alternative splicing events, thereby altering the coding sequence and function of mature mRNAs. RNA splicing modulator-4 is promising for research of neurodegenerative diseases e.g., HuntingtonAAasAasAas disease and cancers.







